L’étude Syde-CAR

Neuromuscular diseases don’t stop progressing when a patient walks out of the clinic. So why should our measurements? Continuous, real-world monitoring captures the daily reality

Wearables and digital health technologies are transforming how we capture real-world outcomes in clinical trials. However, moving to full-scale execution presents significant operational, logistical, and

For years, clinical trials in achondroplasia have relied heavily on annual growth velocity as the primary outcome measure. However, height alone doesn’t tell the full